Gene therapy is a medical field which focuses on the utilisation of the therapeutic delivery of nucleic acid (gene) into patient’s cell as a drug to treat disease.
Very first experiment of gene therapy performed on 4 year old girl with ADA deficiency. This enzyme is very crucial for immune system. Permanent gene therapy can be done by replacement of ADA gene from bone marrow cells of early embryonic stages. It is parmanent and fully successed.
